ALS clinical trials: do enrolled patients accurately represent the ALS population?

Title : ALS clinical trials: do enrolled patients accurately represent the ALS population?

Source : PubMed
ID : 21956723
Authors : Chiò A, Canosa A, Gallo S, Cammarosano S, Moglia C, Fuda G, Calvo A, Mora G; PARALS group.
Year : 2011
Disease Category : Mental disorder
Focused Population : Not Specified
Priori/Posteriori : Posteriori
Single-study Generalibility? : Multiple
Score/Non-Score : Non-score
Tutorial/Method : NHANES_T2D
Compared general demographic and patient characteristics : Yes
Compared disease-specific clinical characteristics : Yes
Compared adverse events : No
Compared outcomes/treatment effect (including survival) : Yes
Trial participants vs. general population (from EHR, survey, a cohort, etc) : Yes
Real-world data sources : trial participants and patients in a registry
Target Population Data Type Levels : National